One's a life saving therapy for kids where 20 kids a year, it's really small number, but 20 kids a year are born with this rare congenital disease where 100% of them died by the age of three if untreated. And The therapy that we got through FDA approval, 70% of those kids now are able to live lives of normal. What was the disease? It's called complete du jour syndrome or congenital athymia. Kids born without a thymus. (49:20–49:25)
CLAIM
Asserts that an FDA-approved therapy allows 70% of affected children to live normal lives.
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