Yeah, I mean there's five drugs, one of them is. So I'll tell you about them. One's a life saving therapy for kids where 20 kids a year, it's really small number, but 20 kids a year are born with this rare congenital disease where 100% of them died by the age of three if untreated. And the therapy that we got through FDA approval, 70% of those kids now are able to live lives of normal. What was the disease? It's called complete du jour syndrome or congenital athymia. (49:11–49:20)
CLAIM
Asserts that 20 children annually are born with a fatal congenital disease if untreated.
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